gene therapy
FDA’s New Era: Diabetes, Blood Pressure, and Gene Therapy Approvals Redefine Medication Safety and Innovation
Recent FDA decisions signal a major shift in medication safety and innovation, with landmark approvals for diabetes, blood pressure, and gene therapies. This article explores how new oral drugs, urgent recalls, and rapid gene therapy authorizations are transforming patient care…
Gene Therapy Breakthrough Slows Huntington’s Disease Progression by 75%
A pioneering gene therapy, AMT-130, is the first to significantly slow Huntington’s disease, marking a historic advance for patients and families.
Sarepta Therapeutics Restructures Amid Challenges with Gene Therapy Elevidys
Sarepta Therapeutics has announced a major restructuring, laying off 36% of its workforce and shifting its research focus amid safety concerns surrounding its gene therapy Elevidys.
SOHM Launches AI Team to Boost Genome Editing Technology
SOHM, Inc., a pharmaceutical and biotechnology company, announced the formation of a dedicated AI team on April 7, 2025, to enhance its ABBIE genome editing system and develop innovative RNA-guided tools for advancements in gene therapy and other fields.